Miplyffa

Miplyffa: Zevra announces price for Niemann-Pick Disease-Type C drug

Zevra Therapeutics' drug, Miplyffa, for treating a rare and fatal genetic disorder will have a… Read More

Miplyffa: US Approves First Treatment for Niemann-Pick Disease-Type C

The US Food and Drug Administration (FDA) approved Miplyffa (arimoclomol), an oral medication for the… Read More